Gain-of-function mutations in fibroblast growth factor receptor (FGFR) genes are known to cause a range of skeletal disorders ...

As of February 17, 2025, 1,028 unique patient prescriptions for Attruby™ have been written by 516 unique prescribers since FDA approval- ...

BridgeBio’s ATTR cardiomyopathy drug, Attruby, achieved promising sales numbers in the weeks after its FDA approval.

Q4 2024 Earnings Call Transcript February 19, 2025 BioMarin Pharmaceutical Inc. beats earnings expectations. Reported EPS is $0.64, expectations were $0.54. Operator: Ladies and gentlemen, thank you ...

As of February 17, 2025, 1,028 unique patient prescriptions for Attruby have been written by 516 unique prescribers since FDA approval - Attruby (acoramidis), the first and only near-complete TTR ...

Infigratinib – FGFR1-3 inhibitor in development for achondroplasia and hypochondroplasia: PROPEL 3, the Phase 3 clinical trial of infigratinib in achondroplasia, the most common form of ...

Depending on the cause, you may feel pain in the front center of your belly, in your back, neck, or your shoulders (especially the right one). The pain may feel sharp or dull. Having liver pain ...

Possible causes of low blood pressure, or hypotension, range from dehydration to a heart condition. Drinking more water may help, but some people will need medication. Changing dietary habits may ...

Dizziness has many possible causes, which may relate to a person’s external environment, the medications they take, or an underlying condition. Dizziness refers to a range of sensations ...